Neuromuscular Research

EXPERTISE:

Neuromuscular Specialist – Clinical trials of a wide variety of potential therapies for inclusion body myositis, amyotrophic lateral sclerosis, myasthenia gravis, and peripheral neuropathy.

ENROLLING STUDIES:

For more information about a study, please contact Yogeet Kaur at (210) 450-0542.

A Randomized, Double-Blind, Multicenter, Placebo-Controlled Phase 3 Study with Open-Label Period to Evaluate the Efficacy and Safety of Inebilizumab in Adults with Myasthenia Gravis (MINT)
https://myastheniagravismintstudy.com/mint/

https://clinicaltrials.gov/ct2/show/NCT04524273?term=mint&recrs=a&draw=2&rank=5

Phase 2 investigation of oral, small molecule Factor D Inhibitor (ALXN-2050 MG-201)
https://alexion.com/our-research/pipeline

https://clinicaltrials.gov/ct2/show/NCT05218096?term=ALXN-2050+MG-201&draw=2&rank=1

A Randomized, Double-Blind, Placebo-Controlled Study to Evaluate the Safety and Efficacy of Pitolisant on Excessive Daytime Sleepiness and Other Non-Muscular Symptoms in Patients with Myotonic Dystrophy Type 1, Followed by an Open-Label Extension (HBS-101-CL-005)
https://www.harmonybiosciences.com/patients

https://clinicaltrials.gov/ct2/show/NCT04886518?term=HBS-101-CL-005&draw=2&rank=1

HEALEY Amyotrophic Lateral Sclerosis (ALS) Platform Trial
https://www.massgeneral.org/neurology/als/research/platform-trial

https://clinicaltrials.gov/ct2/show/NCT04297683?term=platform&recrs=a&cond=ALS+%28Amyotrophic+Lateral+Sclerosis%29&cntry=US&draw=2&rank=1

Clinical Research in Amyotrophic Lateral Sclerosis (ALS) & Related Disorders for Therapeutic Development (CREATE)
https://clinicaltrials.gov/ct2/show/NCT03489278?term=capture&recrs=a&cond=ALS&draw=2&rank=1